KFU. Card publication. RNA Editing for Muscular Dystrophy Therapy

KAZAN
FEDERAL UNIVERSITY

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RNA EDITING FOR MUSCULAR DYSTROPHY THERAPY

Form of presentation

Articles in international journals and collections

Year of publication

2017

Язык

английский

Authors, employees of KFU

Rizvanov Albert Anatolevich, author

Yakovlev Ivan Antonovich, author

Other authors

Deev Roman Vadimovich, author

Isaev Artur Aleksanrovich, author

Bibliographic description in the original language

Yakovlev, I. A. RNA Editing for Muscular Dystrophy Therapy / I. A. Yakovlev, R. V. Deev, A. A. Rizvanov, A. A. Isaev // BioNanoSci. - 2016. - R. 1-4.

Annotation

Due to lack of effective therapies, muscular dystrophies became a focus for gene therapy. Multiple pre-clinical studies have shown successful restoration of dystrofin and dysferlin by RNA editing both in vivo and in vitro, but possibility of a clinical translation is still obscure. A number of new chemicals are being studied, and a search for new techniques is ongoing. This work is intended to give a brief overview of the current state of the RNA editing for treating muscular dystrophies.

Keywords

RNA editing, exon skipping, trans-splicing, duchenne muscular dystrophy, dysferlinopathy

The name of the journal

BioNanoScience

On-line resource for training course

http://dspace.kpfu.ru/xmlui/bitstream/handle/net/109936/RNA_Editing_for_Muscular_Dystrophy_Therapy_BNSC.pdf?sequence=1&isAllowed=y

URL

https://link.springer.com/article/10.1007/s12668-016-0372-0

Please use this ID to quote from or refer to the card

https://repository.kpfu.ru/eng/?p_id=152914&p_lang=2

Resource files

File name	Size (MB)	Format
RNA_Editing_for_Muscular_Dystrophy_Therapy_BNSC.pdf	0,25	pdf	show / download

Full metadata record

Field DC	Value	Language
dc.contributor.author	Rizvanov Albert Anatolevich	ru_RU
dc.contributor.author	Yakovlev Ivan Antonovich	ru_RU
dc.contributor.author	Deev Roman Vadimovich	ru_RU
dc.contributor.author	Isaev Artur Aleksanrovich	ru_RU
dc.date.accessioned	2017-01-01T00:00:00Z	ru_RU
dc.date.available	2017-01-01T00:00:00Z	ru_RU
dc.date.issued	2017	ru_RU
dc.identifier.citation	Yakovlev, I. A. RNA Editing for Muscular Dystrophy Therapy / I. A. Yakovlev, R. V. Deev, A. A. Rizvanov, A. A. Isaev // BioNanoSci. - 2016. - Р. 1-4.	ru_RU
dc.identifier.uri	https://repository.kpfu.ru/eng/?p_id=152914&p_lang=2	ru_RU
dc.description.abstract	BioNanoScience	ru_RU
dc.description.abstract	Due to lack of effective therapies, muscular dystrophies became a focus for gene therapy. Multiple pre-clinical studies have shown successful restoration of dystrofin and dysferlin by RNA editing both in vivo and in vitro, but possibility of a clinical translation is still obscure. A number of new chemicals are being studied, and a search for new techniques is ongoing. This work is intended to give a brief overview of the current state of the RNA editing for treating muscular dystrophies.	ru_RU
dc.language.iso	ru	ru_RU
dc.subject	RNA editing	ru_RU
dc.subject	exon skipping	ru_RU
dc.subject	trans-splicing	ru_RU
dc.subject	duchenne muscular dystrophy	ru_RU
dc.subject	dysferlinopathy	ru_RU
dc.title	RNA Editing for Muscular Dystrophy Therapy	ru_RU
dc.type	Articles in international journals and collections	ru_RU